Risdiplam
Product Specifications
CAS Number
1825352-65-5
Target
DNA/RNA Synthesis
Related Pathways
DNA Damage/DNA Repair, Cell Cycle/Checkpoint
Purity
0.9964
Bioactivity
Risdiplam (RG7916) is a centrally and peripherally distributed and orally administrable small molecule SMN2 pre-mRNA splicing modifier that increases survival motor neuron (SMN) protein levels.
Smiles
Cc1cn2nc(cc(C)c2n1)-c1cc(=O)n2cc(ccc2n1)N1CCNC2(CC2)C1
Molecular Formula
C22H23N7O
Molecular Weight
401.46
Shipping Conditions
Ice Packs
Storage Temperature
-20°C
Available Sizes
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