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Ultevursen (sodium)

Ultevursen sodium is a single-stranded RNA based oligonucleotide that is designed to skip exon 13 in the RNA with the aim to stop vision loss in people that have retinitis pigmentosa due to a mutation in exon 13 of the USH2A gene (encoding usherin) .

Product Specifications

Product Name Alternative

QR-421a (sodium)

UNSPSC

12352208

Target

Others

Type

Oligonucleotides

Related Pathways

Others

Field of Research

Others

Assay Protocol

https://www.medchemexpress.com/ultevursen-sodium.html

Solubility

10 mM in H2O

Smiles

[Ultevursen(sodium)]

Molecular Formula

C273H370N81Na21O144P20S20

Molecular Weight

8372.24 (free acid)

References & Citations

[1]International Nonproprietary Names for Pharmaceutical Substances (INN) . WHO Drug Information, Vol. 36, No. 2, 2022.

Shipping Conditions

Room temperature

Scientific Category

Oligonucleotides

Clinical Information

Phase 3

Curated Selection

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