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Vesleteplirsen (sodium)

Vesleteplirsen (SRP-5051) sodium is a next-generation antisense oligonucleotide of peptide phosphorodiamidate morpholino oligomer (PPMO) . Vesleteplirsen targets exon 51 skipping in Duchenne muscular dystrophy (DMD) [1].

Product Specifications

Product Name Alternative

SRP-5051 (sodium)

UNSPSC

12352208

Target

Others

Type

Oligonucleotides

Related Pathways

Others

Field of Research

Others

Assay Protocol

https://www.medchemexpress.com/srp-5051-sodium.html

Solubility

10 mM in H2O

Smiles

[Vesleteplirsen(sodium)]

Molecular Formula

C404H616N202Na30O130P30

Molecular Weight

11342 (free acid)

References & Citations

[1]Sarepta Therapeutics reports positive clinical results from phase 2 MOMENTUM study of SRP-5051 in patients with Duchenne muscular dystrophy amenable to skipping exon 51. News release. Sarepta Therapeutics. May 3, 2021. Accessed May 4, 2021.

Shipping Conditions

Room temperature

Scientific Category

Oligonucleotides

Clinical Information

Phase 2

Curated Selection

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