Vesleteplirsen (sodium)
Vesleteplirsen (SRP-5051) sodium is a next-generation antisense oligonucleotide of peptide phosphorodiamidate morpholino oligomer (PPMO) . Vesleteplirsen targets exon 51 skipping in Duchenne muscular dystrophy (DMD) [1].
Product Specifications
Product Name Alternative
SRP-5051 (sodium)
UNSPSC
12352208
Target
Others
Type
Oligonucleotides
Related Pathways
Others
Field of Research
Others
Assay Protocol
https://www.medchemexpress.com/srp-5051-sodium.html
Solubility
10 mM in H2O
Smiles
[Vesleteplirsen(sodium)]
Molecular Formula
C404H616N202Na30O130P30
Molecular Weight
11342 (free acid)
References & Citations
[1]Sarepta Therapeutics reports positive clinical results from phase 2 MOMENTUM study of SRP-5051 in patients with Duchenne muscular dystrophy amenable to skipping exon 51. News release. Sarepta Therapeutics. May 3, 2021. Accessed May 4, 2021.
Shipping Conditions
Room temperature
Scientific Category
Oligonucleotides
Clinical Information
Phase 2
Curated Selection
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