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Eteplirsen

Eteplirsen (AVI 4658) is a synthetic antisense oligonucleotide. Eteplirsen can be used for Duchenne muscular dystrophy research[1].

Product Specifications

CAS Number

[1173755-55-9]

Product Name Alternative

AVI 4658

UNSPSC

12352208

Target

Arp2/3 Complex

Type

Oligonucleotides

Related Pathways

Cytoskeleton

Applications

Metabolism-protein/nucleotide metabolism

Field of Research

Metabolic Disease

Assay Protocol

https://www.medchemexpress.com/eteplirsen.html

Purity

98.50

Smiles

[Eteplirsen]

Molecular Formula

C364H569N177O122P30

Molecular Weight

10306.00

References & Citations

[1]Kenji Rowel Q Lim, et al. Eteplirsen in the treatment of Duchenne muscular dystrophy. Drug Des Devel Ther. 2017 Feb 28;11:533-545.

Shipping Conditions

Blue Ice

Storage Conditions

-20°C (Powder, stored under nitrogen, away from moisture)

Scientific Category

Oligonucleotides

Clinical Information

Phase 3

Available Sizes

Curated Selection

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