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Baliforsen

Baliforsen is an antisense oligonucleotide (16 nucleotides) designed to target myotonic dystrophy protein kinase (DMPK) mRNA and research myotonic dystrophy.

Product Specifications

CAS Number

[1698048-23-5]

Product Name Alternative

ISIS 598769; IONIS 598769; BIIB 065; ISIS-DMPK-2.5Rx

UNSPSC

12352208

Target

Ser/Thr Kinase

Type

Oligonucleotides

Related Pathways

Metabolic Enzyme/Protease

Field of Research

Others

Assay Protocol

https://www.medchemexpress.com/baliforsen.html

Purity

95.23

Solubility

H2O : ≥ 100 mg/mL

Smiles

[Baliforsen]

Molecular Formula

C180H240N59O90P15S15

Molecular Weight

5616.00

References & Citations

[1]Wheeler TM, Leger AJ, Pandey SK, et al. Targeting nuclear RNA for in vivo correction of myotonic dystrophy. Nature. 2012;488 (7409) :111-115.

Shipping Conditions

Blue Ice

Storage Conditions

-20°C (Powder, sealed storage, away from moisture)

Scientific Category

Oligonucleotides

Clinical Information

No Development Reported

Available Sizes

Curated Selection

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