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Golodirsen (sodium)

Product Specifications

Product Name Alternative

SRP-4053 (sodium)

UNSPSC Description

Golodirsen sodium is a phosphorodiamidate morpholino oligomer (PMO) that specifically targets exon 53 of dystrophin pre-mRNA. Golodirsen sodium can be used for the research of Duchenne muscular dystrophy (DMD)[1][2].

Target Antigen

Others

Type

Oligonucleotides

Related Pathways

Others

Field of Research

Others

Assay Protocol

https://www.medchemexpress.com/golodirsen-sodium.html

Purity

92.00

Solubility

10 mM in H2O

Smiles

[Golodirsen (sodium)]

Molecular Weight

9222.01

References & Citations

[1]Heo YA. Golodirsen: First Approval. Drugs. 2020 Feb;80(3):329-333.|[2]Scaglioni D, et, al. The administration of antisense oligonucleotide golodirsen reduces pathological regeneration in patients with Duchenne muscular dystrophy. Acta Neuropathol Commun. 2021 Jan 6;9(1):7.

Shipping Conditions

Blue Ice

Storage Conditions

-20°C (Powder, stored under nitrogen, away from moisture)

Product Datasheet

http://file.medchemexpress.com/batch_PDF/HY-132611A/Golodirsen-sodium-DataSheet-MedChemExpress.pdf

Product MSDS

http://file.medchemexpress.com/batch_PDF/HY-132611A/Golodirsen-sodium-SDS-MedChemExpress.pdf

Clinical Information

Phase 4

Available Sizes

Curated Selection

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