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Branaplam (LMI070)

Product Specifications

CAS Number

1562338-42-4

Target

SMN

Applications

DNA Damage/DNA Repair

Smiles

CC1 (CC (CC (N1) (C) C) OC2=NN=C (C=C2) C3=C (C=C (C=C3) C4=CNN=C4) O) C

Molecular Formula

C22H27N5O2

Additionnal Information

Branaplam (LMI070) is a highly selective, small-molecule splicing modulators of survival motor neuron‐2 (SMN2) with an EC50 of 0.02 μM.

Storage Conditions

3 years -20°C powder

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