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Rimigorsen (sodium)

Rimigorsen sodium is an antisense oligonucleotide that induces skipping of exon 44 of the pre-mRNA encoding dystrophin in a Duchenne muscular dystrophy (DMD)

Product Specifications

UNSPSC

12352208

Target

Dystrophin

Related Pathways

Cytoskeleton

Field of Research

Others

Smiles

[Rimigorsen(sodium)]

References & Citations

[1]Method for efficient exon (44) skipping in duchenne muscular dystrophy and associated means. WO2009139630A2

Shipping Conditions

Room temperature

Scientific Category

Oligonucleotides

Clinical Information

No Development Reported

Curated Selection

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