Nucresiran (sodium)
Nucresiran sodium is a siRNA that inhibits hepatic synthesis of both wild-type and variant TTR mRNA.
Product Specifications
Product Name Alternative
ALN-TTRsc04 (sodium)
UNSPSC
12352208
Target
Transthyretin (TTR)
Related Pathways
Neuronal Signaling
Applications
Neuroscience-Neuromodulation
Field of Research
Others
Smiles
[Nucresiran(sodium)]
Molecular Formula
C532H672F8N171Na44O324P43S6
Molecular Weight
17333.80
References & Citations
[1]A Phase 1, Single Ascending Dose Study to Evaluate ALN-TTRsc04, a Next-Generation RNA Interference Therapeutic, in Healthy Participants for Potential Treatment of Transthyretin Amyloidosis
Shipping Conditions
Room temperature
Scientific Category
Oligonucleotides
Clinical Information
Phase 1
Curated Selection
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