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Nucresiran

Nucresiran is a siRNA that inhibits hepatic synthesis of both wild-type and variant TTR mRNA.

Product Specifications

Product Name Alternative

ALN-TTRsc04

UNSPSC

12352208

Target

Transthyretin (TTR)

Related Pathways

Neuronal Signaling

Applications

Neuroscience-Neuromodulation

Field of Research

Others

Smiles

[Nucresiran]

Molecular Formula

C532H716F8N171O324P43S6

Molecular Weight

16366.50

References & Citations

[1]A Phase 1, Single Ascending Dose Study to Evaluate ALN-TTRsc04, a Next-Generation RNA Interference Therapeutic, in Healthy Participants for Potential Treatment of Transthyretin Amyloidosis

Shipping Conditions

Room temperature

Scientific Category

Oligonucleotides

Clinical Information

Phase 1

Curated Selection

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