SLC6A8 corrector 1

SLC6A8 Corrector 1 is an orally active corrector for mutant SLC6A8 variants, capable of crossing the blood-brain barrier. It is utilized in the study of creatine transporter deficiency (CTD) .

IC(C(C(NC)=O)=C(C(C(O)=O)=C1I)I)=C1NC(CCCCCCCCC(NC2=C(C(C(NC)=O)=C(C(C(O)=O)=C2I)I)I)=O)=O.OC[C@@H](O)[C@@H](O)[C@H](O)[C@@H](O)CNC.OC[C@@H](O)[C@@H](O)[C@H](O)[C@@H](O)CNC