SLC6A8 corrector 1
SLC6A8 corrector 1 is an orally active and brain-penetrant mutant SLC6A8 variant corrector. SLC6A8 corrector 1 can be used for the study of creatine transporter deficiency (CTD) [1].
Product Specifications
UNSPSC
12352005
Target
Sodium Channel
Type
Reference compound
Related Pathways
Membrane Transporter/Ion Channel
Applications
Metabolism-protein/nucleotide metabolism
Field of Research
Metabolic Disease
Assay Protocol
https://www.medchemexpress.com/slc6a8-corrector-1.html
Smiles
C[C@@H]1CN(CC[C@@H]1O)C2=CC=NC(C(N[C@H]3C[C@@H]3C4=CC=CC=C4)=O)=C2
Molecular Formula
C21H25N3O2
Molecular Weight
351.44
References & Citations
[1]Lara N Gechijian, et al. Novel Corrector for Variants of SLC6A8: A Therapeutic Opportunity for Creatine Transporter Deficiency. ACS Chem Biol. 2024 Oct 17.
Shipping Conditions
Room temperature
Scientific Category
Reference compound1
Clinical Information
No Development Reported
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