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SMN-C2

SMN-C2 is a selective regulator of SMN2 gene splicing, a risdiplam analogue, a selective RNA-binding ligand that regulates pre-mRNA splicing and acts by binding to SMN2 pre-mRNA.SMN-C2 has the potential to be used in the study of spinal muscular atrophy (SMA) .

Product Specifications

CAS Number

1446311-56-3

Stability

≥ 2 years

Purity

>98% (HPLC)

Weight

417.5

Molecular Formula

C24H27N5O2

Notes

Research use only, not for human use.

Receptor

DNA/RNA Synthesis

Available Sizes

Frequently Asked Questions

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