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Rapirosiran sodium

Rapirosiran sodium is a small interfering RNA conjugated with N-acetylgalactosamine that targets the mRNA of hydroxysteroid 17-β dehydrogenase 13 (HSD17B13) expressed in the liver. Loss-of-function variants of HSD17B13 are associated with a reduced risk of chronic liver diseases.

Product Specifications

CAS Number

2755197-77-2

Storage Conditions

-20°C

Notes

For research use only.

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