RECTAS-2.0
RECTAS-2.0 is a small molecule designed to correct RNA mis-splicing caused by the GLA c.639+919G>A mutation, intended for research in Fabry disease.
Product Specifications
CAS Number
3038234-95-3
Field of Research
Cell Biology, Molecular Biology
Smiles
N (CC1=CC=CO1) C=2C3=C (C (OC[C@H]4CN (C) C (=O) O4) =NC=C3) N=C (Cl) C2
Molecular Formula
C18H17ClN4O4
Molecular Weight
388.805
Storage Conditions
-20°C
Notes
For research use only.
Available Sizes
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