Rugonersen sodium
Rugonersen sodium is an LNA-modified antisense oligonucleotide designed to unsilence UBE3A for Angelman syndrome research. It is applied in preclinical in vitro and in vivo studies to investigate therapeutic strategies for this neurodevelopmental disorder.
Product Specifications
CAS Number
2591588-58-6
Field of Research
Protein Biochemistry
Molecular Formula
C204H235N63Na19O109P19S19
Molecular Weight
6948.00
Storage Conditions
-20°C
Notes
For research use only.
Available Sizes
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