RG7800 tetrahydrochloride
RG7800 hydrochloride is an orally bioavailable small molecule that potently modulates SMN2 splicing (EC50 = 23 nM) and increases SMN protein levels (EC50 = 87 nM) . It is a promising candidate for spinal muscular atrophy research, with demonstrated activity in both cellular assays and preclinical animal models.
Product Specifications
Field of Research
Cell Biology, Molecular Biology
Molecular Formula
C24H32Cl4N6O
Molecular Weight
562.36
Storage Conditions
-20°C
Notes
For research use only.
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