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PTC258

PTC258 is an orally bioavailable small molecule that selectively modulates ELP1 gene splicing to enhance its expression. It has shown activity in both cellular and animal studies, demonstrating good tolerability in mice, and is a useful research tool for investigating splicing modulation and Elongator complex biology.

Product Specifications

CAS Number

2476724-74-8

Field of Research

Cell Biology, Molecular Biology

Smiles

N (CC1=CC=CS1) C2=C3C (C (C) =C (C[C@H] (C) N) S3) =NC (Cl) =C2

Molecular Formula

C16H18ClN3S2

Molecular Weight

351.92

Storage Conditions

-20°C

Notes

For research use only.

Available Sizes

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