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SMN-C2

SMN-C2 is a risdiplam-analogue small molecule that selectively binds SMN2 pre-mRNA to modulate its splicing. This mechanism supports its application in both cellular and animal model research for investigating spinal muscular atrophy (SMA) therapeutics.

Product Specifications

CAS Number

1446311-56-3

Product Name Alternative

DNA Synthesis, DNASynthesis, SMN2, RNA Synthesis, RNASynthesis

Field of Research

Cell Biology, Molecular Biology

Purity

99.01% (May vary between batches)

Smiles

O=C1C (C=2N=C3N (C2) C=C (C) N=C3C) =CC=4C (O1) =CC (=CC4) N5C[C@H] (C) N (CC) CC5

Molecular Formula

C24H27N5O2

Molecular Weight

417.5

Storage Conditions

-20°C

Notes

For research use only.

Available Sizes

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