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Lucerastat

Lucerastat (NBDGJ) is an orally administered glucosylceramide synthase (GCS) inhibitor investigated for Fabry disease. By blocking a key step in sphingolipid biosynthesis, it reduces the accumulation of pathogenic substrates, as demonstrated in relevant cellular and animal models of lysosomal storage disorders.

Product Specifications

CAS Number

141206-42-0

Field of Research

Metabolism Research

Purity

98.00% (May vary between batches)

Smiles

C (CCC) N1[C@H] (CO) [C@H] (O) [C@H] (O) [C@@H] (O) C1

Molecular Formula

C10H21NO4

Molecular Weight

219.28

Storage Conditions

-20°C

Notes

For research use only.

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