NVS-SM2
NVS-SM2 is an orally active small molecule that enhances SMN2 exon 7 inclusion, elevating SMN protein levels in SMA patient fibroblasts and Δ7 mouse myoblasts. This splicing modulator is a valuable research tool for investigating spinal muscular atrophy mechanisms and therapeutic strategies in both cellular and animal models.
Product Specifications
CAS Number
1562333-92-9
Field of Research
Cell Biology, Molecular Biology, Musculoskeletal & Connective Tissue Research
Smiles
CN (C1CC (C) (C) NC (C) (C) C1) c1ccc (nn1) -c1ccc (cc1O) -c1cn[nH]c1
Molecular Formula
C23H30N6O
Molecular Weight
406.52
Storage Conditions
-20°C
Notes
For research use only.
Available Sizes
Frequently Asked Questions
More Discoveries
Explore Other Products
Browse additional items from our catalog
