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NVS-SM2

NVS-SM2 is an orally active small molecule that enhances SMN2 exon 7 inclusion, elevating SMN protein levels in SMA patient fibroblasts and Δ7 mouse myoblasts. This splicing modulator is a valuable research tool for investigating spinal muscular atrophy mechanisms and therapeutic strategies in both cellular and animal models.

Product Specifications

CAS Number

1562333-92-9

Field of Research

Cell Biology, Molecular Biology, Musculoskeletal & Connective Tissue Research

Smiles

CN (C1CC (C) (C) NC (C) (C) C1) c1ccc (nn1) -c1ccc (cc1O) -c1cn[nH]c1

Molecular Formula

C23H30N6O

Molecular Weight

406.52

Storage Conditions

-20°C

Notes

For research use only.

Available Sizes

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