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LMI-070

LMI070 (NVS-SM1, Branaplam) is a potent SMN2 splice modulator (EC50=20 nM) that potential treatment of spinal muscular atrophy (SMA) .Spinal Muscular Atrophy (SMA), Phase 2 Clinical.

Product Specifications

CAS Number

1562338-42-4

Product Name Alternative

NVS-SM1 | Branaplam

Purity

>98% (HPLC)

Solubility

DMSO: 6.12 mg/mL

Smiles

CC1 (CC (CC (N1) (C) C) OC2=NN=C (C=C2) C3=C (C=C (C=C3) C4=CNN=C4) O) C

Molecular Formula

C22H27N5O2

Molecular Weight

393.4821

Storage Conditions

Storage temperature: -20°C. Stability: ≥ 2 years

Notes

For research use only.

Other Product Names

Phenol, 5- (1H-pyrazol-4-yl) -2-[6-[ (2,2,6,6-tetramethyl-4-piperidinyl) oxy]-3-pyridazinyl]-

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