Givosiran
Product Specifications
CAS Number
1639325-43-1
Target
Others
Related Pathways
Others
Bioactivity
Givosiran (ALN-AS1) is a small interfering RNA (siRNA) compound that specifically targets hepatic aminolevulinate synthase 1 (ALAS1) messenger RNA (mRNA) to downregulate its expression, thereby inhibiting the accumulation of neurotoxic ?-aminolevulinic acid and porphobilinogen levels, with significant potential for further research on acute intermittent porphyria.
Shipping Conditions
Cool pack
Storage Temperature
-20°C
Available Sizes
Curated Selection
Explore Other Products
Discover premium biology products from our extensive collection of 20M+ items
