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Givosiran

Product Specifications

CAS Number

1639325-43-1

Target

Others

Related Pathways

Others

Bioactivity

Givosiran (ALN-AS1) is a small interfering RNA (siRNA) compound that specifically targets hepatic aminolevulinate synthase 1 (ALAS1) messenger RNA (mRNA) to downregulate its expression, thereby inhibiting the accumulation of neurotoxic ?-aminolevulinic acid and porphobilinogen levels, with significant potential for further research on acute intermittent porphyria.

Shipping Conditions

Cool pack

Storage Temperature

-20°C

Available Sizes

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