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Nusinersen

Product Specifications

CAS Number

1258984-36-9

Target

DNA/RNA Synthesis

Related Pathways

Cell Cycle/Checkpoint|||DNA Damage/DNA Repair

Purity

0.9862

Bioactivity

Nusinersen (nusinersen) is an antisense oligonucleotide (ASO) for the treatment of pediatric and adult spinal muscular atrophy (SMA) that alters the way the SMN2 gene is processed and increases the production of SMN proteins, which are deficient in SMA patients.

Shipping Conditions

Cool pack

Storage Temperature

-20°C

Available Sizes

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