Nusinersen
Product Specifications
CAS Number
1258984-36-9
Target
DNA/RNA Synthesis
Related Pathways
Cell Cycle/Checkpoint, DNA Damage/DNA Repair
Purity
0.9862
Bioactivity
Nusinersen (nusinersen) is an antisense oligonucleotide (ASO) for the treatment of pediatric and adult spinal muscular atrophy (SMA) that alters the way the SMN2 gene is processed and increases the production of SMN proteins, which are deficient in SMA patients.
Shipping Conditions
Ice Packs
Storage Temperature
-20°C
Available Sizes
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