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Lucerastat

Product Specifications

CAS Number

141206-42-0

Target

Transferase

Related Pathways

Metabolism

Purity

0.98

Bioactivity

Lucerastat?NBDGJ? is an orally available inhibitor of Glucosylceramide Synthase (GCS) with therapeutic potential for Fabry disease. GCS is a key enzyme in sphingolipid synthesis and inhibition of its activity reduces the accumulation of harmful substrates.

Smiles

C(CCC)N1[C@H](CO)[C@H](O)[C@H](O)[C@@H](O)C1

Molecular Formula

C10H21NO4

Molecular Weight

219.28

Shipping Conditions

Cool pack

Storage Temperature

-20°C

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