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Ataluren

Product Specifications

CAS Number

775304-57-9

Target

Autophagy, CFTR

Related Pathways

Membrane transporter/Ion channel, Autophagy

Purity

0.9984

Bioactivity

Ataluren (PTC124) is a novel, orally administered drug that targets nonsense mutations. Ataluren is approved for use by the European Medicines Agency to treat Duchenne Muscular Dystrophy in patients aged 5 years and older who are able to walk.

Smiles

FC1=C(C2=NC(=NO2)C3=CC(C(O)=O)=CC=C3)C=CC=C1

Molecular Formula

C15H9FN2O3

Molecular Weight

284.24

Shipping Conditions

Ice Packs

Storage Temperature

-20°C

Available Sizes

Frequently Asked Questions

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